New Breakthrough in Haemophilia Treatment
Recently, Indian researchers have successfully developed a gene therapy treatment for severe haemophilia A, showing promising results in a trial, with five patients reporting no bleeding episodes for over a year.
The findings have been published in a peer-reviewed journal in December 2024.
- The gene therapy trial was conducted on five patients in Tamil Nadu, who have not reported any bleeding episodes for an average follow-up period of 14 months.
- The treatment uses a lentivirus vector to introduce the clotting factor gene, which is considered a safer alternative to the adenovirus vector used in Roctavian, a gene therapy approved by ....